Working Toward a Cure

Doctors at Nationwide Children’s Hospital in Columbus, Ohio have conducted research that leads them to believe that a cure for MPS II has been discovered. Dr. Fu and Dr. McCarty have conducted years of research and are relying on parent-led organizations to raise the funds needed to carry the drug development process through clinical trials. Human clinical trials involve administering the drug in a controlled environment to gather data on efficacy. This is usually done before making the drug available to all affected patients.

In order to continue the work to save these childrens lives, $450,000 are needed by November 2017 and another $950,000 by February 2018. These funds will cover expenses such as securing the facility where the clinical trials will be held, along with building of vectors that will be used to introduce the cure to our little SuperHeroes. The remaining balance of the $2.5 million dollars will be used to cover medical costs, room and boarding costs, and miscellaneous costs for the patients who will be participating in the clinical trial. If all deadlines are met, Dr. Fu and Dr. McCarty hope to start clinical trials by end of Summer 2018.

Meet the Doctors working to save the lives of those affected by Hunter Syndrome (MPS II)

The Research Institute at Nationwide Children’s Hospital
700 Childrens Drive
Columbus, OH 43205

Douglas M. McCarty, PhD

Douglas M. McCarty, PhD

Center for Gene Therapy  
Principal Investigator

Neurology
Principal Investigator

Neurology Residency
Faculty

Neuromuscular Disorders
Principal Investigator

Neurosciences
Principal Investigator

Haiyan Fu, PhD

Haiyan Fu, PhD

Center for Gene Therapy
Principal Investigator

MPS Articles and Events

MPS SuperHero Donations

We have collected $60,203.65 of our $2,500,000.00 target. It is 2.41% of our goal for the BE A SUPERHERO. SAVE A LIFE. campaign

2.41%

Recent Donations

August 23 2017
$1,000.00
SunTrust Bank
August 15 2017
$25.00
Anonymous 
August 14 2017
$250.00
Vivian Santiago
August 02 2017
$50.00
Anonymous 
July 31 2017
$25.00
Patricia  Muñoz